Sophia Zilber

Company: Cure Mito foundation

Job title: Board Member

Seminars:

Fireside Chat: Building an Ecosystem for Stakeholders to Strengthen Patient Advocacy for Regulatory Success 3:00 pm

Uniting patient advocates, regulators and health technology assessors to provide patients with predictive disease indications Creating an alliance with regulators at the early stages of discovery to embrace the unique pathway to drug approval for mitochondrial diseases Looking beyond the epidemiology to maximize the potential of drug developers and commercial successRead more

day: CONFERENCE DAY TWO

Patient Registries: Thinking Beyond the Data Collection for Expanding Therapeutic Avenues 2:30 pm

Delving into Cure Mito’s global patient registry for Leigh syndrome to uncover what makes it unique Assessing registry data for regulatory use and recognition Evaluating the addition of a new registry: A meaningful contribution or a redundant effort? Read more

day: CONFERENCE DAY TWO