Improving Patient Recruitment for Rare Mitochondrial Disease Clinical Trials to Rigorously Demonstrate Drug Efficacy
Time: 2:50 pm
day: Day Two
Details:
- Establishing the value of clinical care within clinical trials to maintain trust and improve recruitment for clinical trials in mitochondrial disease drug development
- Incorporating patient voice into decision making for mitochondria-disease specific endpoints
- Focusing on quality of life, patient experience, and pain management throughout mitochondrial therapy development, advancing clinical readiness for mitochondrial disease