Advancing Preclinical Modelling of Inherited & Rare Mitochondrial Diseases
Time: 12:00 pm
day: Pre-Conference Day
Details:
To date, animal mitochondrial DNA has remained resistant to transfection and has limited the availability of models for rare diseases.
Workshop highlights include:
- Discover the key hurdles towards developing truly predictive models to improve translation and drug efficacy in humans
- Explore the newest mitochondrial transfer strategies for developing animal models to recapitulate system-wide energy crisis of mitochondria
- Understand how this can be applied to the drug development pipeline and predicting efficacy and safe therapeutic windows
